Meet members of the ITF Therapeutics team to learn more about their organization and next steps to support the availability of DUVYZAT.
This pre-recorded webinar delves into the world of travel with special guests, Marissa Penrod and Adam Malone. Not only is Marissa an expert on traveling with Duchenne, but Adam is a travel advisor who also happens to live with the condition. We are also be joined by Alan Chaulet, who is the Vice President of All Wheels Up which is a non-profit that is working to increase awareness for safer and more dignified accessible travel. Together, they provide invaluable insights, tips, and stories that will leave you feeling inspired and empowered to embark on your very own adventure.
Dyne Therapeutics will present initial clinical data, first released on January 3rd, 2024, from the DELIVER trial of DYNE-251 in patients with Duchenne muscular dystrophy (DMD) who are amenable to exon 51 skipping.
Join PTC Therapeutics and CureDuchenne for this prerecorded webinar to hear important information regarding Emflaza, PTC Cares and the programs that support the Duchenne community. Topics include:Understanding Your PrescriptionHow to Ensure Your Son […]
Join us for this pre-recorded presentation and Q&A discussing to learn about a new FDA-approved treatment for Duchenne muscular dystrophy. During the session, Catalyst Pharmaceuticals will provide an overview of […]
Join us for this pre-recorded presentation and Q&A discussing Dyne’s Phase 1/2 clinical trial, DELIVER, evaluating DYNE-251 for the treatment of individuals with Duchenne muscular dystrophy (DMD) who are amenable […]
Join Edgewise’s Chief Scientific Officer and Chief Medical Officer to discuss the clinical development program for EDG-5506, a myosin modulator, that aims to prevent muscle damage in Becker and Duchenne […]
VILTEPSO: AN FDA-APPROVED TREATMENT FOR PATIENTS WITH DUCHENNE MUSCULAR DYSTROPHY (DMD) AMENABLE TO EXON 53 SKIPPING This is a pre-recorded webinar with CureDuchenne, NS Pharma and guest speaker Dr. Mathula […]
REGENXBIO’s Senior Director and Clinical Development Lead, Dr. Jahannaz Dastgir and Dr. Veerapandiyan from Arkansas Children’s Hospital share updates about RGX-202, an investigational gene therapy for the treatment of Duchenne […]
