THE CURE IS WITHIN REACH 

20 years ago, we set out to get Duchenne research out of labs and into clinics. Our next 3-5 years will be focused on translating these experimental drugs into approved therapies leading to curative treatments.

OUR IMPACT

  • Funded 17 research projects that have advanced to human clinical trials
  • Funded multiple projects aimed at overcoming the limitations of gene therapy 
  • Contributed early funding to the first FDA-approved Duchenne drug 
  • Pioneered the first and only Duchenne physical and occupational therapist certification program 
  • Successfully implemented a hospital-based pilot to screen newborns for Duchenne 
  • Created an innovative biobank and data registry, facilitating data sharing between patients and researchers 

We know you will want to be a part of this countdown to a cure and ask you to please lend your support.

Support CureDuchenne Today!