The FDA will make a decision whether or not to grant full approval of Sarepta’s gene therapy, Elevidys, by June 21,2024.
Fat embolism syndrome (FES) is a potentially life-threatening condition that can be triggered by bone fractures.
Finding the Right One: Advice from Experts on Dating with a Disability
By Jacob Gapko Jacob Gapko is 46 years old and has Duchenne muscular dystrophy. He uses a power wheelchair and non-invasive ventilation 24/7. He has a B.S. in physics and minors […]
Justin Skeesuck, a 48-year-old Idahoan featured in the documentary “I’ll Push You,” started losing the use of his hands in 2010. So, in 2012, he moved to Italy. For a […]
Dyne Therapeutics Announces Positive Initial Clinical Data from ACHIEVE Trial in DM1 Patients and DELIVER Trial in DMD Patients
This year, our CureDuchenne blogs ran the gamut from FDA approvals to overcoming adversity to books and movies that represent people with disabilities to how to stay happy and healthy. […]
Agamree (vamorolone) was recently approved by the FDA, and Catalyst explains the new steroid and how to get it in this CureDuchenne Webinar.
Books are a gateway for us to unlock our imaginations. To see ourselves in the characters that captivate our attention. To let our mind wander to places that wouldn’t have […]