CureDuchenne Blog

Books About Duchenne For Children and Parents

Enjoy this hand-picked selection of books about Duchenne muscular dystrophy for children and parents. This list was shared at the 2022 FUTURES National Conference in Orlando, FL. (Duchenne Community Bookstore […]

CureDuchenne Joins AMP BGTC

CureDuchenne joins forces with NIH, FDA, and private organizations to increase effective gene therapies for rare diseases CureDuchenne is delighted to be a partner in the Accelerating Medicines Partnership Bespoke […]

WMS 2021 Day 5: Late-breaking News

In WMS 2021’s final day and “late-breaking news” session, Capricor Therapeutics announced positive final data from its Phase 2 HOPE-2 clinical trial in Duchenne patients treated with CAP-1002. HOPE-2 was […]

WMS 2021 Day 4: Clinical Trial Updates

WMS 2021 on Thursday, September 23rd was a full day of oral and poster presentations, and we’ll highlight some Duchenne clinical trial updates covered. Solid Biosciences – SGT-001 micro-dystrophin gene […]

WMS 2021 Day 3: Opening Lecture and Debates

WMS 2021’s agenda on Wednesday, September 22nd was not so much about specific diseases, but rather major and timely research themes across all of biology.  The day started with a […]

WMS 2021 Day 1: Industry Symposia

Monday, September 20th was the first day of the WMS 2021 Virtual Congress, and a day devoted to symposia sponsored by various companies developing therapeutic treatments for neuromuscular disorders.  Most […]