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Terapia Génica ELEVIDYS
Terapia Génica ELEVIDYS: Actualización Comunitaria Más Reciente con Sarepta Therapeutics Watch HERE
Dyne Webinar: Positive Topline Results from DELIVER trial in Exon 51 DMD
A presentation with Dr. Doug Kerr, Chief Medical Officer at Dyne Therapeutics. Dr. Kerr shares topline results from the DELIVER clinical trial, along with new long-term data showing sustained benefits […]
Insmed’s ASCEND Study and INS1201, an Investigational Gene Therapy for Duchenne Muscular Dystrophy
Watch HERE
CureDuchenne Cares Webinar: Optimizing Cardiac Outcomes in Duchenne
CureDuchenne and Andreas S. Barth, MD, PhD, FAHA, for a community webinar about Optimizing Cardiac Outcomes in Duchenne. Watch HERE
WEBINAR: Avidity EXPLORE44-OLE Functional Data Update
Avidity reports multiple functional improvements with Del-zota for individuals with Duchenne amenable to skipping exon 44. Watch HERE
WEBINAR: Edgewise
A Fireside Chat with Mike Kelly and Edgewise Therapeutics: A Duchenne Program Update Wednesday, September 3, 2025 WATCH HERE
Edgewise Therapeutics: Focused on Muscle Disease
Developing a novel therapeutic designed to protect muscle in Becker and Duchenne muscular dystrophy Watch HERE
REGENXBIO AFFINITY DUCHENNE: Trial of Investigational RGX-202 Gene Therapy
In this webinar, Dr. Naz Dastgir, Executive Medical Director and Clinical Development Lead for RGX-202 at REGENXBIO, shared information on the active and enrolling AFFINITY DUCHENNE trial and how families […]
Craft Your Story
Crafting Your Story for Awareness, Connection, and Change Webinar. Watch HERE