Duchenne gene therapy Archives

REGENXBIO Reports New Positive Interim Data from Phase I/II AFFINITY DUCHENNE Gene Therapy Trial

March 11, 2026

REGENXBIO GENE THERAPY RGX-202, an investigational gene therapy for Duchenne, continues to show a favorable safety profile with no serious adverse events, no liver injury signals, and reductions in key […]

Decoding Gene Therapy for Duchenne

July 7, 2023

While there is currently no cure for Duchenne muscular dystrophy, gene therapy has the potential to target the underlying genetic cause of many mono genetic diseases and could potentially benefit […]