Donate
info@cureduchenne.org(949) 872-2552
EventsContact
Cart
×

No products in the cart.

CureDuchenne
Moble Nav Icon
  • Cure
    • CureDuchenne Link
    • Research Overview
    • Research Terms
    • Exon Skipping
    • Clinical Trials
  • Care
    • COVID-19 Resources
    • Newly Diagnosed
    • Clinic
    • Steroid Use
    • Emergency Care
    • Resource Library
    • DME Guide
    • Medical ID Bracelets
    • Navigating School
    • Occupational Therapy
    • Physical Therapy
    • For Families
    • - Find a Physical Therapist
    • - Pool Activities
    • - Stretching
    • For Physical Therapists
    • - PT Certification
    • - Professional Courses
    • For Clinics
  • Community
    • CureDuchenne CARES
    • CureDuchenne FUTURES
    • CureDuchenne Champions
    • Family Stories
    • Events
    • Previous Webinars
    • Family Fundraisers
  • About Us
    • Mission
    • Vision
    • About Duchenne
    • Blog
    • Board of Directors
    • Sponsors
    • Events & Webinars
    • News Center
    • - Press Releases
    • - Partner News
  • CD Ventures
    • About CD Ventures
    • Our Impact
  • Get Involved
    • Donate
    • More Ways to Give
    • Fundraise
    • Shop
    • Fundraising Events
    • - Ladies Luncheon Austin
    • - Getzlaf Golf Shootout | Orange County, CA
    • - Napa in Newport | Orange County, CA
  • Donate
  • All
  • Cure Duchenne Blog
  • Press Releases
  • CureDuchenne In The News
  • Research
REGENXBIO Duchenne microdystrophin

Positive data reported for REGENXBIO’s AAV8-delivered microdystrophin, RGX-202

November 18, 2024

CureDuchenne is delighted to share the positive updates from REGENXBIO on their Phase 1/2 open-label clinical trial of RGX-202, an AAV8-delivered microdystrophin with an extended C-terminal domain.  RGX-202 demonstrated robust […]

Read More

Genethon’s Duchenne Muscular Dystrophy Gene Therapy GNT0004 Produces Expression of Microdystrophin in Phase 1/2/3 Trial

June 24, 2024

Genethon reported positive results from its AAV-microdystrophin treatment trial in Europe.  The three participants receiving the study’s higher dose (3×1013vg/kg) showed that an average of 54% of muscle fibers were […]

Read More

  • About

    • Mission
    • About Duchenne MD
    • Blog
    • Store
    • News Center

  • Get Involved

    • Donate
    • Fundraising
    • Attend an Event

  • CureDuchenne

    • 100 Bayview Circle, Suite 5600
      Newport Beach, CA 92660
      (949) 872-2552
      info@cureduchenne.org

  • Get Connected

PRIVACY POLICY | TERMS OF USE | INDIRECT COST POLICY | TAX INFO

CureDuchenne is a 501c3 registered tax-exempt nonprofit organization. Federal Tax ID: #20-0299958 | ©2025 CureDuchenne. All rights reserved.

Please be advised that the contents within the CureDuchenne site include a compilation of articles, advisements, and references from the community. CureDuchenne does not provide medical advice nor is CureDuchenne a medical provider. The intent of this shared content is to serve as a point of reference for informational purposes. Please refer to your health care provider(s) for your individualized, specific care management needs. The CureDuchenne website may contain links to external websites that are not provided and/or maintained by or in any way affiliated with CureDuchenne. CureDuchenne recommends that you review the terms of service and privacy policies of these external websites before entering. Please note that CureDuchenne does not guarantee the accuracy, relevance, timeliness, or completeness of any information on these external websites.

We use cookies to ensure that we give you the best experience on our website. By continuing to use this site you are agreeing to accept our use of cookies. For more information about cookies please visit our Privacy Policy page.I Agree