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PTC FDA Duchenne Nonsense mutation

FDA will review resubmission of PTC’s Translarna for Duchenne caused by nonsense mutation

October 30, 2024

CureDuchenne is pleased to share that PTC Therapeutics has announced that the FDA has accepted for review the New Drug Application (NDA) for Translarna (ataluren) for the treatment of Duchenne […]

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PTC Therapeutics Provides Key Regulatory Updates

March 19, 2024

PTC Therapeutics Provides Key Regulatory Updates

Read More

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