CureDuchenne is pleased to share the following updates from Pfizer pertaining to the on-going multicenter Phase II clinical trial of the investigational compound, domagrozumab (PF-06252616) in boys with Duchenne muscular […]
Guest blog by Paul Miller Our son Hawken was diagnosed with Duchenne in the fall of 2002. Debra and I rolled up our sleeves and began a journey we had […]
As a community, we need to continue our efforts to find a cure for every single person impacted by Duchenne. That means funding research that treats all aspects of the […]
Yesterday the House of Representatives passed the draft of the 21st Century Cures Act. It is slated for a vote in the Senate early next week. The […]
NEWPORT BEACH, Calif., December 1, 2016 – The date for the highly anticipated 2017 Napa in Newport Wine Auction has been set for March 4 at the Ritz-Carlton, Laguna Niguel. […]
Newport Beach, CA Nov. 28, 2016 — It has taken decades, millions of research dollars, heartache and hopefulness to reach a critical milestone of the first FDA approved pharmaceutical treatment […]
Thanksgiving is more than a chance to appreciate what we have. It’s also about taking the time to appreciate the people who help us in our journey, those who share […]
My heart was beating so fast, anxiety creeping into my body. It felt like everything stopped. I can’t remember her exact words, but I distinctly remember the fear that took […]
The final decisions could be made today on the 21st Century Cures Act and the OPEN ACT – a provision that could be transformational for rare disease patients. CureDuchenne […]