Event Proceeds Will Advance Research and Support the CureDuchenne Clinic within the Neuromuscular Program at Rady Children’s Health Orange County NEWPORT BEACH, California (September 19, 2025) – CureDuchenne, a global […]
Edgewise Therapeutics, which received early funding from CureDuchenne, has reported positive results in its sevasemten program for Becker and Duchenne muscular dystrophies. New open-label data in Becker from the MESA trial demonstrated […]
Inspired by “The Remarkable Life of Ibelin” documentary, Players Around the World Uniteto Honor Mats Steen and Drive Groundbreaking Research and Vital Care NEWPORT BEACH, California (February 5, 2025) – […]
Upcoming Events Offer Treatment Updates and Essential Resources to Support Families and Enhance Quality of Life NEWPORT BEACH, Calif., January 31, 2025 – CureDuchenne, a global leader in advancing research and […]
By Debra Miller, Founder and CEO of CureDuchenne I’m honored to share two transformative events that embody both the resilience of the human spirit and the strength of our community: […]
Read a message from our founder and CEO The recently released award-winning Netflix documentary “The Remarkable Life of Ibelin,”* highlights the life of Mats Steen, a Norwegian World of Warcraft […]
CureDuchenne welcomes the recent initiative the Food and Drug Administration (FDA) has taken to improve efficiencies in drug development, manufacturing, and the review process for new drug applications that incorporate […]
See the previous update from June 22, 2023 here FDA Grants Traditional Approval for Ambulatory Individuals and Accelerated Approval for Non-Ambulatory Individuals to Sarepta Therapeutics’ ELEVIDYS Gene Therapy for Duchenne […]
We are blessed that our son Momo joined our family through adoption. It was a long road to bring him home that led us to understand that God’s plans are […]
