Cart
×
Update from Pfizer for the CIFFREO trial and Pfizer’s open-label DAYLIGHT trial to treat Duchenne
See the below letter to the community
NS Pharma Announces FDA Clearance to InitiatePhase II Study forNS-089/NCNP-02, an Exon 44 Skipping Candidate for the Treatment of Duchenne Muscular Dystrophy
PARAMUS, NJ: April 14, 2023,–NS Pharma, Inc. announced today the U.S. Food & Drug Administration (FDA)has agreed to the planned Phase II study of NS-089/NCNP-02 for Duchenne muscular dystrophy. NS-089/NCNP-02 […]
CureDuchenne and PicnicHealth Announce Real-World Evidence-Focused Partnership to Incorporate Participant Medical Records into CureDuchenne Link
CureDuchenne and PicnicHealth Announce Real-World Evidence-Focused Partnership to Incorporate Participant Medical Records into CureDuchenne Link
FDA Update on the Accelerated Approval of Sarepta’s Gene Therapy
As you may have read in the news, Sarepta Therapeutics today announced an update from the FDA on the review of SRP-9001, Sarepta’s experimental gene therapy for Duchenne muscular dystrophy. They shared the following information:
Dyne Therapeutics Receives FDA Orphan Drug and Rare Pediatric Designations
Dyne Therapeutics, who received early funding from CureDuchenne, has received FDA Orphan Drug and Rare Pediatric Designations for DYNE-251 for the Treatment of Duchenne Muscular Dystrophy.
First CureDuchenne Clinic Opens in Greater Dallas to Provide Specialized Care for Underserved Duchenne Muscular Dystrophy Patients
First CureDuchenne Clinic Opens in Greater Dallas to Provide Specialized Care for Underserved Duchenne Muscular Dystrophy Patients
CureDuchenne Ventures Invests in hC Bioscience and its Novel tRNA-Based Therapeutic Approach for Duchenne Muscular Dystrophy
CureDuchenne Ventures Invests in hC Bioscience and its Novel tRNA-Based Therapeutic Approach for Duchenne Muscular Dystrophy
Hawken Miller is a journalist, bringing his experience writing for outlets like The Washington Post and BioNews, along with his personal experience living with Duchenne muscular dystrophy, to CureDuchenne. Learn more about Hawken here.
Decoding Clinical Trials
Find a clinical trial that works for you! Clinicaltrials.gov, managed by the U.S. National Library of Medicine, includes 439,599 research studies in 50 states and 221 countries. Many of those […]