Justin Skeesuck, a 48-year-old Idahoan featured in the documentary “I’ll Push You,” started losing the use of his hands in 2010. So, in 2012, he moved to Italy. For a […]
Dyne Therapeutics Announces Positive Initial Clinical Data from ACHIEVE Trial in DM1 Patients and DELIVER Trial in DMD Patients
This year, our CureDuchenne blogs ran the gamut from FDA approvals to overcoming adversity to books and movies that represent people with disabilities to how to stay happy and healthy. […]
Agamree (vamorolone) was recently approved by the FDA, and Catalyst explains the new steroid and how to get it in this CureDuchenne Webinar.
Books are a gateway for us to unlock our imaginations. To see ourselves in the characters that captivate our attention. To let our mind wander to places that wouldn’t have […]
Read Astellas community letter below:
Solid Biosciences Announces IND Clearance by FDA for Duchenne Muscular Dystrophy Gene Therapy Candidate SGT-003
Mother of two boys with Duchenne shares how she’s successfully advocated for her children with a rare disease as a mama bear.
Shopping for someone with a physical disability can seem difficult as this holiday season rolls around. They may not have the same strength or dexterity as other kids and/or adults […]