Dr. Olson Presents on Gene Editing

Today, Dr. Eric Olson, PhD, Chair of Molecular Biology at UT Southwestern, was honored to give a presentation at the American Society of Gene & Cell Therapy (ASGCT) 2017 meeting in Washington DC for the George Stamatoyannopoulos Lecture series.

Dr. Olson presented new research showing how gene editing technologies like CRISPR/Cas9 and Cpf-1 can be used to correct mutations that lead to Duchenne muscular dystrophy. Dr. Olson’s presentation highlighted the importance and therapeutic value of advancing work in gene editing therapies for Duchenne, and showed how gene editing technology could potentially be used to treat Duchenne patients with point mutations, deletions, duplications, and pseudo-exons.

Dr. Olson is excited to continue translation of his exciting pre-clinical research in Duchenne into a clinical therapy through a biotech company he has collaborated with CureDuchenne to form called Exonics Therapeutics.

Click here for more information on CRISPR/Cas9 or view the video.   Donate to help advance this research that could potentially correct a majority of the mutations in Duchenne.

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