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Pfizer
Pfizer Industry Presentation
Allie Guider
Field Medical Director, Rare Disease Duchenne Muscular Dystrophy Gene Therapy
Pfizer
Video
2023 FUTURES Breakout Session: Growth and Transformation (ages 9-16)
Let’s discuss:
- Growing pains and puberty
- Introducing wheelchairs and equipment
- Preparing for a bright future: confidence, independence, and hobbies
- Neurology concerns
- Cardiology concerns
- Pulmonology concerns
- Managing Mobility
Sheryl Marrazzo
Duchenne Mother, Grandmother and Advocate
4 Jake's Sake | CureDuchenne
Danielle Forrest, OTR, OTD
Occupational Therapist III
Children’s Health and Rehabilitation Services
Dr. Aravindhan Veerapandiyan
Pediatric Neurologist
Arkansas Children's Hospital
Oscar "Hank" Mayer, MD
Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia
Merick Yamada, MD
Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center
Video
2023 FUTURES Breakout Session: Overcoming Everyday Challenges
How to talk to others about unique challenges like marriage and family dynamics, talking to your kids about Duchenne, and other everyday obstacles that many families in this community face.
Video
2023 FUTURES: Advancing Care Across the Duchenne Journey Part 2
Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.
Jennifer Wallace Valdes, PT
CureDuchenne Certified Physical Therapist
CureDuchenne Physical Therapy Program
Danielle Forrest, OTR, OTD
Occupational Therapist III
Children’s Health and Rehabilitation Services
Angelena Edwards, MD - Speakers
Pediatric Urologist
University of Iowa Stead Family Children's Hospital
Kindann Fawcett, PhD
Post Doctoral Fellow
University of Arkansas for Medical Sciences
Austin Edenfield, ATP
Quantum Product & Technical Education Manager
Pride Mobility
Video
2023 FUTURES: Advancing Care Across the Duchenne Journey Part 1
Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.
Dr. Aravindhan Veerapandiyan
Pediatric Neurologist
Arkansas Children's Hospital
Kent Williams, MD
Pediatric Gastroenterologist
Nationwide Children's Hospital
Oscar "Hank" Mayer, MD
Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia
Merick Yamada, MD
Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center
Video
2023 FUTURES: Trailblazers The Future of Care Panel
A panel discussion featuring leading healthcare providers that are making a positive impact on variety of aspects of care for Duchenne.
Pradeep P.A. Mammen, MD, FACC, FAHA
Associate Professor of Medicine and Co-Director
Senator Paul D. Wellstone Muscular Dystrophy Cooperative Research Center, Director for Translational Research for the Advanced Heart Failure and Transplant Cardiology Program, UT Southwestern Medical Center
Diana Castro, MD
Associate Professor of Pediatrics, Neurology and Neurotherapeutics
University of Texas Southwestern
Richard Parad, MD, MPH
Associate Professor of Pediatrics / Department of Pediatric Newborn Medicine Harvard Medical School Department of Pediatrics / Brigham and Women's Hospital
Video
2023 FUTURES: Welcome & Saturday Keynote Address
Justin & Patrick are back! From wheelchair races in the courtyard to personally connecting with families, parents, caregivers and individuals with Duchenne, their experience with the community last year was hugely impactful on them. The duo is back to share new stories from their last accessible journey through Camino de Santiago and encourage others the find and foster purpose – no matter the circumstances.
Justin Skeesuck and Patrick Gray
Inspirational Keynote Speakers
I'll Push You
Video
2023 FUTURES: RNA targeted Therapeutics Sessions Part 2
Continued updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.
Mark Stahl, MD, PhD
Senior Medical Director, Clinical Development
Avidity Biosciences
Dania Porco, MS, MBA, CGC
Director in Clinical Science BioMarin Pharmaceutical Inc.
Video
2023 FUTURES: Gene Therapy and Gene Editing Sessions
A brief primer on the gene therapy and gene editing approach to treating Duchenne, and updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.
Alison Mcvie-Wylie, PhD
Vice President, Disease Area Executive, DMD
Vertex Pharmaceutical
Patrick Gonzalez, PhD
Senior Director of Clinical Science Solid Biosciences
Teji Singh, MD
Vice President, Head of Clinical Development Sarepta Therapeutics
Video
