2023 FUTURES

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2023 FUTURES National Conference

2023 FUTURES Breakout Session: Growth and Transformation (ages 9-16)

Let’s discuss:

  • Growing pains and puberty
  • ​Introducing wheelchairs and equipment
  • ​Preparing for a bright future: confidence, independence, and hobbies
  • Neurology concerns
  • Cardiology concerns
  • Pulmonology concerns
  • Managing Mobility

Sheryl Marrazzo

Duchenne Mother, Grandmother and Advocate

4 Jake's Sake | CureDuchenne

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Danielle Forrest, OTR, OTD

Occupational Therapist III

Children’s Health and Rehabilitation Services

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Dr. Aravindhan Veerapandiyan

Pediatric Neurologist

Arkansas Children's Hospital

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Oscar "Hank" Mayer, MD

Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia

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Merick Yamada, MD

Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center

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Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years

2023 FUTURES Breakout Session: Overcoming Everyday Challenges

How to talk to others about unique challenges like marriage and family dynamics, talking to your kids about Duchenne, and other everyday obstacles that many families in this community face.

Hawken Miller

Content Strategist

CureDuchenne

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Doug Levine, PT

CureDuchenne Certified Physical Therapist

CureDuchenne

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Barry and Luci Nilson

CureDuchenne Champions and Parents

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Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years

2023 FUTURES: Advancing Care Across the Duchenne Journey Part 1

Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.

Dr. Aravindhan Veerapandiyan

Pediatric Neurologist

Arkansas Children's Hospital

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Kent Williams, MD

Pediatric Gastroenterologist

Nationwide Children's Hospital

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Oscar "Hank" Mayer, MD

Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia

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Merick Yamada, MD

Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center

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Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years

2023 FUTURES: Advancing Care Across the Duchenne Journey Part 2

Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.

Jennifer Wallace Valdes, PT

CureDuchenne Certified Physical Therapist

CureDuchenne Physical Therapy Program

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Danielle Forrest, OTR, OTD

Occupational Therapist III

Children’s Health and Rehabilitation Services

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Angelena Edwards, MD - Speakers

Pediatric Urologist

University of Iowa Stead Family Children's Hospital

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Kindann Fawcett, PhD

Post Doctoral Fellow

University of Arkansas for Medical Sciences

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Austin Edenfield, ATP

Quantum Product & Technical Education Manager

Pride Mobility

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2023 FUTURES: CureDuchenne’s 20th Anniversary: Contributions to the Cure

A warm welcome from the Miller Family, and an informative presentation on CureDuchenne’s timeline of contributions and investments, and how these inform our future vision.

Debra Miller and Paul Miller

Founders

CureDuchenne

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Hawken Miller

Content Strategist

CureDuchenne

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2023 FUTURES: Friday Keynote – On the Cutting Edge of Research

The science and research-focused day of FUTURES will begin with an engaging keynote panel featuring key opinion leaders who will discuss the successes, learnings, challenges, and future of this disease space.

Michael Kelly, PhD

Chief Scientific Advisor

CureDuchenne

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Emil Kakkis, PhD

CEO & President

Ultragenyx Pharmaceutical

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Alison Mcvie-Wylie, PhD

Vice President, Disease Area Executive, DMD

Vertex Pharmaceutical

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Dan Levy, MD

VP and Development Head, Rare Neurology Pfizer

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Carsten Bönnemann, MD

Chief, Neuromuscular and Neurogenetic Disorders of Childhood Section National Institute of Neurological Disorders and Stroke/NIH

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Kevin Flanigan, MD

Director, Center for Gene Therapy Nationwide Children's Hospital

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2023 FUTURES: Gene Therapy and Gene Editing Sessions

A brief primer on the gene therapy and gene editing approach to treating Duchenne, and updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.

Alison Mcvie-Wylie, PhD

Vice President, Disease Area Executive, DMD

Vertex Pharmaceutical

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Jahannaz Dastgir, DO

Clinical Development Lead REGENXBIO

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Patrick Gonzalez, PhD

Senior Director of Clinical Science Solid Biosciences

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Teji Singh, MD

Vice President, Head of Clinical Development Sarepta Therapeutics

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Dan Levy, MD

VP and Development Head, Rare Neurology Pfizer

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2023 FUTURES: New Science Sessions

A session that highlights novel and pre-clinical research in Duchenne.

Dave Anderson, PhD

Chief Scientific Officer CodeBio

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Ranjan Batra, PhD

Senior Vice President, Research & Development Locanabio

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Stan Froehner, PhD

Founder and Chairman Myosana Therapeutics

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Peixin Zhu, PhD

VP of R&D Tevard Biosciences

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Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years