2023 FUTURES: Preserving Muscle Sessions

A brief primer on the muscle preservation and anti-inflammatory treatment approach to Duchenne, and updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.

Abby Bronson

Vice President, Patient Advocacy & External Innovation

Edgewise Therapeutics

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Robert Halter, PharmD

Field Medical Director, South/Southwest Santhera Pharmaceuticals

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Karyn Koladicz, MD

Executive Medical Director for Medical Affairs, Neurology PTC Therapeutics

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Linda Marbán , PhD

President, CEO and Director Capricor Therapeutics

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2023 FUTURES: RNA targeted Therapeutics Sessions Part 1

A brief primer on the RNA-targetd therapeutic approach to treating Duchenne, and updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.

Ash Dugar, PhD

Senior Vice President, Medical Affairs

Dyne Therapeutics

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Adam Gold, PhD

Medical Science Liasion

NS Pharma

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Kevin Flanigan, MD

Director, Center for Gene Therapy Nationwide Children's Hospital

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Karin Lucas, Ph.D

West Medical Science Liaison Team Lead, Global Medical Affairs Sarepta Therapeutics

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Christian Werner, MD

Executive Director, Global Medical Affairs, and Global Duchenne Muscular Dystrophy Lead PTC Therapeutics

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2023 FUTURES: New Science Sessions

A session that highlights novel and pre-clinical research in Duchenne.

Dave Anderson, PhD

Chief Scientific Officer CodeBio

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Ranjan Batra, PhD

Senior Vice President, Research & Development Locanabio

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Stan Froehner, PhD

Founder and Chairman Myosana Therapeutics

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Peixin Zhu, PhD

VP of R&D Tevard Biosciences

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2023 FUTURES: Friday Keynote – On the Cutting Edge of Research

The science and research-focused day of FUTURES will begin with an engaging keynote panel featuring key opinion leaders who will discuss the successes, learnings, challenges, and future of this disease space.

Michael Kelly, PhD

Chief Scientific Advisor

CureDuchenne

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Emil Kakkis, PhD

CEO & President

Ultragenyx Pharmaceutical

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Alison Mcvie-Wylie, PhD

Vice President, Disease Area Executive, DMD

Vertex Pharmaceutical

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Dan Levy, MD

VP and Development Head, Rare Neurology Pfizer

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Carsten Bönnemann, MD

Chief, Neuromuscular and Neurogenetic Disorders of Childhood Section National Institute of Neurological Disorders and Stroke/NIH

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Kevin Flanigan, MD

Director, Center for Gene Therapy Nationwide Children's Hospital

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2023 FUTURES: CureDuchenne’s 20th Anniversary: Contributions to the Cure

A warm welcome from the Miller Family, and an informative presentation on CureDuchenne’s timeline of contributions and investments, and how these inform our future vision.

Debra Miller and Paul Miller

Founders

CureDuchenne

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Hawken Miller

Content Strategist

CureDuchenne

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Beginning the Duchenne Journey 

From FUTURES 2023

 

  • Coping as a Caregiver
  • Communicating Duchenne to your child/family
  • ​Preparing for a bright future: play, communicate, and appropriate exercise
  • Neurological concerns
  • Introducing Stretching and Equipment
  • Role of Social Work
  • Duchenne’s Impact on Nutritional Health and Habits

Kayla Richards, LMSW

Social Worker

UT Health Austin Pediatric Neurosciences at Dell Children's

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Doug Levine, PT

CureDuchenne Certified Physical Therapist

CureDuchenne

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Leslie Porter

Family, Duchenne Advocate

Family, Duchenne Advocate

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Diana Castro, MD

Associate Professor of Pediatrics, Neurology and Neurotherapeutics

University of Texas Southwestern

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Kindann Fawcett, PhD

Post Doctoral Fellow

University of Arkansas for Medical Sciences

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