CureDuchenne Link™ is a Centralized Hub with Data and Biosamples for Researchers Around the World Newport Beach, CA (June 18, 2021) – CureDuchenne, a leading global nonprofit focused on finding […]
Currently, there is a clear paucity of information to guide exercise prescription for patients with DMD. While clinical concerns based on the notion that excessive exercise may exacerbate the disease […]
Our youngest son, Henry, was diagnosed with Duchenne in August 2011 – shortly before his 3rd birthday. It was a fluke test that shocked even the doctors as it was […]
Dear Duchenne Community, All of us at Italfarmaco would like to thank the families participating in the Phase 3 EPIDYS trial and in the open label extension study of givinostat […]
Newport Beach, CA, December 21, 2020 – CureDuchenne, a leading global nonprofit focused on funding and finding a cure for Duchenne muscular dystrophy, announced today a new initiative to deliver […]
Dear Committee Members, On behalf of individuals living with Duchenne muscular dystrophy, their families, and caregivers served by CureDuchenne, I am writing to urge the Committee to include individuals with Duchenne in its recommendations for sub-populations to receive approved or authorized COVID-19 […]
November 9, 2020 Results from all cohorts of PRECISION-HD1 and PRECISION-HD2 clinical trials and initial OLE data on track for 1Q 2021Dosing in three new clinical trials with novel compounds […]
-Collaboration combines Solid’s differentiated microdystrophin construct and Ultragenyx’s HeLa PCL manufacturing platform for use with AAV8 and variants- -Solid receives $40 million upfront via equity investment at a premium; up […]
Dear U.S. Duchenne community, As you know from our previous updates, the SIDEROS clinical trial is fully enrolled and Santhera has been working with the Food and Drug Administration (FDA) […]
