My name is Debra Miller, founder and CEO of CureDuchenne, and the mother of an incredible son, Hawken, who has Duchenne muscular dystrophy. I’m here today to represent the voice of patient advocacy organizations serving those impacted by Duchenne – all of whom are in support of the accelerated approval of SRP-9001.
Newport Beach, Calif. (May 11, 2023) – CureDuchenne Ventures announced funding for MyoGene Bio, LLC, a biotech company developing a novel gene editing therapy for Duchenne muscular dystrophy (DMD). […]
CureDuchenne Ventures announces an investment in Insmed Inc. to support the development of INS1201, their next generation intracerebroventricular (ICV) delivered AAV to directly address limitations of current gene therapy approaches.
CureDuchenne’s Second Annual “Napa in Miami” Wine Tasting and Auction Raises More Than $1.2 Million to Help Find a Cure for Duchenne Muscular Dystrophy
CureDuchenne and PicnicHealth Announce Real-World Evidence-Focused Partnership to Incorporate Participant Medical Records into CureDuchenne Link
CureDuchenne’s Second Annual “Napa in Miami” Wine Tasting and Auction Raises More Than $1.2 Million to Help Find a Cure for Duchenne Muscular Dystrophy
First CureDuchenne Clinic Opens in Greater Dallas to Provide Specialized Care for Underserved Duchenne Muscular Dystrophy Patients
Savvy Business Veteran Ryan T. Meardon Bolsters Executive Team, Bringing High-Level Strategic Planning and Leadership to Global Rare Disease Nonprofit Newport Beach, Calif. – February 1, 2023 – CureDuchenne, a global […]
Southern California’s Premier Wine Event Brought Together Acclaimed Napa Valley Vintners Under One Roof to Raise Funds for CureDuchenne NEWPORT BEACH Calif., November 10, 2022 – CureDuchenne and Vintner Chair Dana Estates hosted the Eighth […]
