REGENXBIO is recruiting participants aged 4-11 years old for their microdystrophin gene therapy trial, as well as participants aged 0-11 years for an observational study to understand the prevalence of anti-AAV8 and AAV9 antibodies in boys with Duchenne. See the below REGENXBIO press release
You can advance the care, treatment and cure for Duchenne muscular dystrophy. Contributions in any amount can truly make a difference and can be credited to a fundraiser or event from the list below.
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