Presentations on early-stage research and development companies working on approaches to address the unmet therapeutic needs in the Duchenne community.
A Duchenne emergency case study, the steps to take, and the signs to watch for. From implementing an emergency plan and following it to effective communication with the Emergency Room to get the care you need. A review of the cautions and a proactive plan of care from specialists.
A moderated panel discussion focusing on the potential challenges and complications of AAV therapy and the clinical strategies to make dosing AAV more successful.
Breakout Session: A Steroid Discussion, One Disease, Many Paths
With more choices available, what should families consider? A panel breakout session to help families navigate the steroid journey, make informed choices, and proactively respond to side-effects.
Diana Castro, MD
Associate Professor of Pediatrics, Neurology and Neurotherapeutics
A warm welcome from Debra, Paul and Hawken, and an informative presentation on CureDuchenne’s timeline of contributions and investments, and how these inform our future vision.
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