Diana Castro, MD

Title: Founder and Director of the Neurology and Neuromuscular Care Center

Bio: Since completing training in pediatric neuromuscular medicine, Dr. Castro has conducted multiple clinical research trials, as principal investigator in Spinal Muscular Atrophy (SMA), Duchenne Muscular Dystrophy (DMD), and Charcot-Marie-Tooth (CMT). The pediatric neuromuscular research group at Children’s Health is very active, currently running over 18 clinical trials, including natural history and treatment-related studies. Dr. Castro is the director of the Pediatric Neuromuscular Division.

Avidity Biosciences: Presentation and discussion on initial data from EXPLORE44 Clinical Trial

This webinar, hosted by CureDuchenne and Avidity Biosciences, presents the initial data from the EXPLORE 44 clinical trial. The trial evaluates the efficacy and safety of Dalzota (AOC 1044) for treating Duchenne muscular dystrophy (DMD) in patients amenable to exon 44 skipping. Key findings include a significant increase in exon skipping and dystrophin production, with a notable reduction in creatine kinase levels, indicating potential muscle health improvements. The discussion also covers the future plans for the trial and the urgency to advance treatment options for DMD patients.

Michael Kelly, PhD

Chief Scientific Advisor

CureDuchenne

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Diana Castro, MD

Founder and Director of the Neurology and Neuromuscular Care Center

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Husam Younis, PhD

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Sarah Boyce

President and CEO of Avidity Biosciences

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Beginning the Journey - diagnosed 0-3 yearsSpreading Wisdom - diagnosed 6+ years