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2021 FUTURES: Keynote Panel
An inspiring conversation about living in the moment with a rare diagnosis.
Video
2023 FUTURES Breakout Session: Growth and Transformation (ages 9-16)
Let’s discuss:
- Growing pains and puberty
- Introducing wheelchairs and equipment
- Preparing for a bright future: confidence, independence, and hobbies
- Neurology concerns
- Cardiology concerns
- Pulmonology concerns
- Managing Mobility
Sheryl Marrazzo
Duchenne Mother, Grandmother and Advocate
4 Jake's Sake | CureDuchenne
Danielle Forrest, OTR, OTD
Occupational Therapist III
Children’s Health and Rehabilitation Services
Dr. Aravindhan Veerapandiyan
Pediatric Neurologist
Arkansas Children's Hospital
Oscar "Hank" Mayer, MD
Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia
Merick Yamada, MD
Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center
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2023 FUTURES Breakout Session: Overcoming Everyday Challenges
How to talk to others about unique challenges like marriage and family dynamics, talking to your kids about Duchenne, and other everyday obstacles that many families in this community face.
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2023 FUTURES: Advancing Care Across the Duchenne Journey Part 1
Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.
Dr. Aravindhan Veerapandiyan
Pediatric Neurologist
Arkansas Children's Hospital
Kent Williams, MD
Pediatric Gastroenterologist
Nationwide Children's Hospital
Oscar "Hank" Mayer, MD
Medical Director, Pulmonary Function Testing Laboratory Children's Hospital of Philadelphia
Merick Yamada, MD
Pediatric Cardiologist Fetal Care Center Dallas | Neurology and Neuromuscular Care Center
Video
2023 FUTURES: Advancing Care Across the Duchenne Journey Part 2
Relevant healthcare providers discuss the most critical advancements and recommendations in their specialty, and answer questions from the audience.
Jennifer Wallace Valdes, PT
CureDuchenne Certified Physical Therapist
CureDuchenne Physical Therapy Program
Danielle Forrest, OTR, OTD
Occupational Therapist III
Children’s Health and Rehabilitation Services
Angelena Edwards, MD - Speakers
Pediatric Urologist
University of Iowa Stead Family Children's Hospital
Kindann Fawcett, PhD
Post Doctoral Fellow
University of Arkansas for Medical Sciences
Austin Edenfield, ATP
Quantum Product & Technical Education Manager
Pride Mobility
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2023 FUTURES: Collaborating for a Cure
A session about how to get involved with CureDuchenne Link.
Learn more about CureDuchenne Link and how to participate please visit: cureduchenne.org/cureduchenne-link
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2023 FUTURES: CureDuchenne’s 20th Anniversary: Contributions to the Cure
A warm welcome from the Miller Family, and an informative presentation on CureDuchenne’s timeline of contributions and investments, and how these inform our future vision.
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2023 FUTURES: Friday Keynote – On the Cutting Edge of Research
The science and research-focused day of FUTURES will begin with an engaging keynote panel featuring key opinion leaders who will discuss the successes, learnings, challenges, and future of this disease space.
Alison Mcvie-Wylie, PhD
Vice President, Disease Area Executive, DMD
Vertex Pharmaceutical
Carsten Bönnemann, MD
Chief, Neuromuscular and Neurogenetic Disorders of Childhood Section National Institute of Neurological Disorders and Stroke/NIH
Kevin Flanigan, MD
Director, Center for Gene Therapy Nationwide Children's Hospital
Video
2023 FUTURES: Gene Therapy and Gene Editing Sessions
A brief primer on the gene therapy and gene editing approach to treating Duchenne, and updates from relevant companies in the space. These presentations will be followed by a moderated Q&A opportunity.
Alison Mcvie-Wylie, PhD
Vice President, Disease Area Executive, DMD
Vertex Pharmaceutical
Patrick Gonzalez, PhD
Senior Director of Clinical Science Solid Biosciences
Teji Singh, MD
Vice President, Head of Clinical Development Sarepta Therapeutics
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