CureDuchenne Link is a centralized data hub which combines clinical data, biosamples, and patient reported data for individuals with Duchenne and Becker muscular dystrophy, as well as carriers. Information and samples provided by participants are coded and available for use by approved researchers across the world.
Esta presentación se enfoca en manejar los desafíos asociados con un diagnóstico de Duchenne.
Esta sesión de la conferencia brinda información sobre las terapias emergentes más allá de la restauración de la distrofina, así como actualizaciones/anuncios de las empresas en este espacio.
Vice President, Patient Advocacy & External Innovation
Edgewise Therapeutics
Vice President of Clinical Development
Capricor Therapeutics
This resource provides an in-depth view of mental health practices like mindfulness and values-based gratitude practices for adults with Duchenne navigating life’s unique obstacles.
A brief overview of the rationale behind next generation technology, as well as presentations from the companies in this space. Moderated discussion included.
This resource provides an introduction to palliative care’s function, benefits, and how it fits into the multidisciplinary care model for Duchenne.
Associate Professor of Pediatrics
University of California San Francisco Benioff's Children's Hospitals
Este panel discutirá los portadores genéticos de Duchenne, cómo comunicar el diagnóstico a otros y las experiencias con la planificación familiar.
Presidenta, Coalición Latinoamericana DMD/DMB
Coalición Latinoamericana DMD/BMD
Consejera Genética Certificada
Hospital de Niños de San Antonio
Pfizer Industry Presentation
Field Medical Director, Rare Disease Duchenne Muscular Dystrophy Gene Therapy
Pfizer
