Physical Therapy: Early Intervention
This resource discusses the benefits of early intervention therapy, what to expect from a PT/OT, basic activity modifications, stretching and orthoses for children.
This resource discusses the benefits of early intervention therapy, what to expect from a PT/OT, basic activity modifications, stretching and orthoses for children.
Esta sesión está dirigida a familias/cuidadores de niños y adolescentes con Duchenne. Cubre cuatro pilares del viaje temprano de Duchenne: atención multidisciplinaria, esteroides, nutrición y participación en ensayos clínicos, y es seguido por una sesión de discusión/preguntas y respuestas.
Post Doctoral Fellow
University of Arkansas for Medical Sciences
Professor and Associate Chair
University of Florida, Department of Pediatrics
Pediatric Neurologist
Arkansas Children's Hospital
Associate Professor of Pediatrics, Neurology and Neurotherapeutics
University of Texas Southwestern
This session is intended for families/caregivers of children and adolescents with Duchenne. It covers four pillars of the early Duchenne journey: Multidisciplinary Care, Steroids, Nutrition, and Involvement in Clinical Trials, and is followed by a discussion/Q&A session.
Professor and Associate Chair
University of Florida, Department of Pediatrics
Associate Professor of Pediatrics, Neurology and Neurotherapeutics
University of Texas Southwestern
Post Doctoral Fellow
University of Arkansas for Medical Sciences
This session is intended for families/caregivers of teens and adults with Duchenne. It covers four pillars of the transitional Duchenne journey: Continuity of Care, GI-related Care, Medical Privacy, and School/Career/Hobbies, and is followed by a discussion/Q&A session.
Associate Professor of Medicine and Co-Director
Senator Paul D. Wellstone Muscular Dystrophy Cooperative Research Center, Director for Translational Research for the Advanced Heart Failure and Transplant Cardiology Program, UT Southwestern Medical Center
Director, Payer Relations
Little Hercules Foundation
Pediatric Gastroenterologist
Nationwide Children's Hospital
Este recurso proporciona información sobre las actividades en la piscina y las rutinas de estiramiento adecuadas.
RGX-202: REGENXBIO’s investigational gene therapy for the treatment of Duchenne Muscular Dystrophy presented by: Johannaz (Naz) Dastgir, DO, Senior Director, Clinical Development Lead at REGENXBIO
A program update on RGX-202, REGENXBIO’s investigational gene therapy program for the treatment of Duchenne.
Contact: Duchenne@regenxbio.com or patientadvocacy@regenxbio.com
Senior Director, Clinical Development Lead
REGENXBIO
Santhera Industry Presentation
Global Program Lead and Head of Medical Affairs
Santhera Pharmaceuticals
Sarepta Pipeline Update for the Duchenne Community
Contact Information for Patient Affairs Team: advocacy@sarepta.com