This is a pre-recorded webinar with CureDuchenne, NS Pharma and guest speaker Dr. Mathula Thangarajh.
Topics include:
• Clinical evidence to support early initiation of DMD treatment
• The role of exon skipping in the treatment of DMD
• The efficacy of VILTEPSO for the treatment of DMD
• The safety and tolerability profile of VILTEPSO
This webinar, in partnership with the University of Kansas Medical Center, explores topics like achieving milestones, quality of life, and setting goals in families navigating Duchenne muscular dystrophy. The panelists also discuss how to incorporate quality of life metrics into clinical care.
Professor of Neurology
University of Kansas Medical Center
Clinical Assistant Professor
University of Kansas Medical Center
Medical Student
University of Kansas Medical Center
An overview of CureDuchenne Link.
Senior Director of Clinical Operations | Director, CureDuchenne Link
CureDuchenne
This resource provides guides to proper massage and aquatic therapy techniques, safe transfers, and stretching routines approved by our CureDuchenne Certified Physical Therapists.
Hear from CureDuchenne’s Chief Scientific Advisor on our research support and priorities.
This resource presents a conversation about family dynamics, communication strategies and how to cope as a family unit navigating a Duchenne diagnosis.
Social Worker and Neuro-behavioral Health Specialist
University of Utah Health
This resource presents information on how to cope with mental heath issues like anxiety and PTSD after a medical emergency.
This resources provides a introduction to the common multidisciplinary care team for Duchenne and their individual functions, as well as tips on coordinating this team-based approach.
Child Neurologist and Neuromuscular Section Head
Children’s Hospital of Philadelphia
This resource presents information on the clinical trial process, common clinical trial terms, updated trial processes due to telehealth, and more.
